OUR ACTIONS FOR THE RESEARCH
Although clinical trials are in progress, no treatment is still on the market and unfortunately new children are worldwide diagnosed, but also in Geneva.
actual research
Research | Company | MPS Type | statut |
Gene therapy | Abeona | Sanfilippo A & B | Clinical |
Gene therapy | Lysogene | Sanfilippo A | Clinical |
Chaperon | Dorphan | Morquio & GM1 | pre-clinical |
Imunosugar | CMU – Geneva | Heparanase | fundamental research |
stopped research
Research | Company | MPS Type | statut |
Greffe de la moelle | Compagnie | Type de MPS | stopped |
Modulation pharmacologique activité lysosomale | Compagnie | Type de MPS | stopped |
Chaperons chimiques N-acétylglucosaminidase | Compagnie | Type de MPS | stopped |